Emapalumab for Severe Hepatitis

(SHIELD Trial)

SC
MF
Overseen ByMaria Frazer
Age: < 65
Sex: Any
Trial Phase: Phase 2
Sponsor: Children's Healthcare of Atlanta
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

The goal of this study is to see whether a medicine called emapalumab, a monoclonal antibody, is safe and works well for patients aged 1 year and older who have indeterminate severe hepatitis with T-cell activation and have not responded well to steroids or still need them.

This study has a Screening Cohort and an Intervention Cohort.

The Screening Cohort will enroll patients with severe hepatitis of all etiologies to observe and collect research samples. Patients enrolled on the Screening Cohort will be asked to participate on the Intervention Cohort if they develop steroid-refractory/ dependent indeterminate severe hepatitis (iSH-T). Additionally, patients may bypass the Screening Cohort and enroll directly in the Intervention Cohort if they already meet its eligibility criteria. Patients in the Intervention Cohort will be treated with emapalumab.

Are You a Good Fit for This Trial?

This trial is for people aged 1 year and older with severe hepatitis that hasn't improved with steroids or who still need steroids. It focuses on those whose hepatitis shows signs of T-cell activation, regardless of the cause.

Inclusion Criteria

Intervention Cohort: Evidence of T-cell activation at initial diagnosis indicated by sIL2R > 2× ULN, or CXCL9 > 5× ULN, or CD8+ T-cell infiltration in the liver
Intervention Cohort: INR < 2.0 without evidence of hepatic encephalopathy
I have severe liver injury with very high ALT levels in the past week.
See 4 more

Exclusion Criteria

Screening Cohort: Any condition impairing informed consent/assent or protocol compliance
Intervention Cohort: History of severe hypersensitivity or allergy to any component of the study regimen
Intervention Cohort: Patient or parent/guardian unable to give informed consent or comply with treatment protocol
See 19 more

What Are the Treatments Tested in This Trial?

Interventions

  • Emapalumab

Trial Overview

The study is testing emapalumab, a monoclonal antibody medicine, to see if it is safe and effective for treating severe hepatitis in patients not responding well to steroid treatment. Patients may be observed first or start treatment right away if they qualify.

How Is the Trial Designed?

1

Treatment groups

Experimental Treatment

Group I: Intervention CohortExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Children's Healthcare of Atlanta

Lead Sponsor

Trials
172
Recruited
108,000+

Sobi, Inc.

Industry Sponsor

Trials
14
Recruited
1,000+