37 Participants NeededMy employer runs this trial

ATR 1072 for Cardiomyopathy

PR
Overseen ByPatient Recruitment Coordinator
Age: 18+
Sex: Any
Trial Phase: Phase 1 & 2
Sponsor: Atrium Therapeutics
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)

What You Need to Know Before You Apply

What is the purpose of this trial?

ATR 1072 is an investigational medicine being studied in adults with PRKAG2 Syndrome. This study will evaluate the safety of ATR 1072 and how the body processes the drug. Researchers will also assess how ATR 1072 affects PRKAG2 activity and measures of heart disease.

Are You a Good Fit for This Trial?

This trial is for adults aged 18 to 65 who have PRKAG2 Syndrome confirmed by genetic testing and show symptoms of the condition. Participants must be able and willing to follow study procedures, including a heart tissue biopsy.

Inclusion Criteria

I am between 18 and 65 years old.
I have a PRKAG2 gene variant found by genetic testing.
I am willing and able to have a heart tissue biopsy.
See 2 more

What Are the Treatments Tested in This Trial?

Interventions

  • ATR 1072

Trial Overview

The study is testing ATR 1072, an experimental drug, in people with PRKAG2 Syndrome. It aims to see how safe the drug is, how the body handles it, and its effects on heart disease related to this syndrome.

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Group I: Part B - Expansion Cohort at the Recommended Phase 2 DoseExperimental Treatment1 Intervention
Group II: Part A - MAD Dose Escalation Description Three sequential ascending doseExperimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Atrium Therapeutics

Lead Sponsor