Naive T Cell Deplete Grafts for Bone Marrow Failure

Not yet recruiting at 1 trial location
ML
Overseen ByMadhavi Lakkaraja, MD, MPH
Age: < 65
Sex: Any
Trial Phase: Phase 2
Sponsor: Fred Hutchinson Cancer Center
No Placebo GroupAll trial participants will receive the active study treatment (no placebo)
Prior Safety DataThis treatment has passed at least one previous human trial

What You Need to Know Before You Apply

What is the purpose of this trial?

This phase II trial investigates how well a naive T cell depleted graft work for the reduction of graft versus host disease in patients with non-malignant diseases requiring hematopoietic cell transplantation. Giving chemotherapy and total-body irradiation before a donor peripheral blood stem cell transplant helps stop the growth of cells in the bone marrow, including normal blood-forming cells (stem cells) and cancer cells. It may also stop the patient's immune system from rejecting the donor's stem cells. When the healthy stem cells from a donor are infused into the patient, they may help the patient's bone marrow make stem cells, red blood cells, white blood cells, and platelets. The donated stem cells may also replace the patient's immune cells and help destroy any remaining cancer cells.

Who Is on the Research Team?

ML

Madhavi Lakkaraja, MD, MPH

Principal Investigator

Fred Hutch Cancer Center

Are You a Good Fit for This Trial?

This trial is for people with non-cancerous blood and immune system disorders, such as bone marrow failure or primary immunodeficiency, who need a stem cell transplant from a donor. Participants should not have active cancer.

Inclusion Criteria

Patient with suitable HCT donor
I am 13 or older and have given consent, or my guardian has given permission.
I am between 6 months and 5 years old.
See 1 more

Exclusion Criteria

I am allergic to tacrolimus or MMF.
I do not have an uncontrolled infection that would prevent a transplant.
I have severe combined immunodeficiency (SCID).
See 11 more

What Are the Treatments Tested in This Trial?

Interventions

  • ALLOGENEIC CD34+ ENRICHED AND CD45RA- DEPLETED PBSCs

Trial Overview

The study tests if using donor stem cells that are specially processed to remove certain naive T cells (CD45RA-) can lower the risk of graft versus host disease after transplantation. All participants receive chemotherapy and total-body irradiation before the transplant.

How Is the Trial Designed?

2

Treatment groups

Experimental Treatment

Group I: Arm B (HLA-matched related or matched unrelated donor )Experimental Treatment1 Intervention
Group II: Arm A (HLA-Haploidentical or mismatched unrelated donor)Experimental Treatment1 Intervention

Find a Clinic Near You

Who Is Running the Clinical Trial?

Fred Hutchinson Cancer Center

Lead Sponsor

Trials
583
Recruited
1,341,000+